Fund Holdings — Palo Alto Investors LP

Total Portfolio Value:
$723.72M
Total Bought:
$41.52M
Total Sold:
$92.22M
Net Transaction:
-$50.70M
Notable People:
Palo Alto Investors Gp Llc
Securities
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SharesValue
Q1 2026
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Q2 2026
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Change
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Q1 2026
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Q2 2026
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Weight (%)
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Change
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PTC Therapeutics, Inc.(PTCT)921,607918,846-2,761$62.79M$74.95M10.36%+$12.16M
ACADIA PHARMACEUTICALS INC2,872,6952,864,096-8,599$63.95M$72.46M10.01%+$8.52M
Insmed Incorporated(INSM)415,269413,980-1,289$67.90M$44.14M6.10%-$23.77M
Mirum Pharmaceuticals, Inc.(MIRM)325,175348,808+23,633$30.04M$40.83M5.64%+$10.80M
ANAPTYSBIO INC638,161603,489-34,672$35.39M$40.74M5.63%+$5.34M
BioMarin Pharmaceutical Inc.(BMRN)685,182682,777-2,405$38.71M$39.07M5.40%+$362.6K
Dyne Therapeutics, Inc.(DYN)1,652,9721,647,521-5,451$29.97M$36.59M5.06%+$6.62M
United Therapeutics Corporation(UTHR)62,80962,587-222$37.24M$33.91M4.69%-$3.33M
Disc Medicine, Inc.(IRON)401,719416,646+14,927$25.69M$30.47M4.21%+$4.79M
Biogen Inc.(BIIB)140,719140,279-440$25.80M$30.31M4.19%+$4.51M
Iovance Biotherapeutics, Inc.(IOVA)6,349,5635,296,209-1,053,354$22.29M$22.03M3.04%-$254.7K
Ultragenyx Pharmaceutical Inc.(RARE)596,495596,4950$12.50M$19.92M2.75%+$7.42M
NovoCure Limited(NVCR)1,280,4391,280,4390$13.96M$19.40M2.68%+$5.44M
Syndax Pharmaceuticals, Inc.(SNDX)864,986864,9860$20.21M$18.91M2.61%-$1.30M
ANNEXON INC2,948,0902,948,0900$16.33M$16.83M2.33%+$501.2K
BICARA THERAPEUTICS INC550,408550,4080$10.95M$16.34M2.26%+$5.39M
CareDx, Inc.(CDNA)531,870531,8700$9.23M$15.16M2.09%+$5.93M
Celldex Therapeutics, Inc.(CLDX)296,408399,856+103,448$9.40M$14.88M2.06%+$5.48M
COMPASS THERAPEUTICS INC1,514,5045,831,813+4,317,309$8.01M$12.77M1.76%+$4.76M
Alkermes plc(ALKS)242,560242,5600$8.58M$12.71M1.76%+$4.13M
FIRST TRACKS BIOTHERAPEUTICS0603,489+603,489$0$12.14M1.68%+$12.14M
PROTHENA CORP PLC
SHS
1,208,5681,143,155-65,413$11.75M$11.19M1.55%-$555.8K
Travere Therapeutics, Inc.(TVTX)230,453167,525-62,928$6.85M$9.52M1.32%+$2.67M
Taysha Gene Therapies, Inc.(TSHA)1,391,3821,391,3820$6.22M$9.48M1.31%+$3.26M
ACLARIS THERAPEUTICS INC1,613,4301,613,4300$6.05M$8.54M1.18%+$2.48M
Agios Pharmaceuticals, Inc.(AGIO)213,601213,6010$7.23M$7.93M1.10%+$700.6K
CAPRICOR THERAPEUTICS INC229,763229,7630$6.98M$5.53M0.76%-$1.45M
ALIGN TECHNOLOGY INC41,52031,389-10,131$7.12M$5.29M0.73%-$1.82M
Oruka Therapeutics, Inc.(ORKA)59,98533,546-26,439$2.94M$3.19M0.44%+$250.3K
Xenon Pharmaceuticals Inc.(XENE)51,34551,3450$2.99M$3.10M0.43%+$113.5K
Neurocrine Biosciences, Inc.(NBIX)18,11718,1170$2.39M$3.05M0.42%+$666.6K
EDWARDS LIFESCIENCES CORP33,64033,6400$2.69M$3.04M0.42%+$349.2K
Stoke Therapeutics, Inc.(STOK)84,63184,6310$2.76M$2.77M0.38%+$13.5K
Cytokinetics, Incorporated(CYTK)32,19532,1950$2.12M$2.74M0.38%+$620.7K
PYXIS ONCOLOGY INC1,010,510864,277-146,233$1.48M$2.60M0.36%+$1.13M
EHEALTH INC1,482,7971,482,7970$1.91M$2.21M0.31%+$296.6K
CRISPR Therapeutics AG(CRSP)39,60539,6050$1.88M$2.16M0.30%+$276.0K
SAGIMET BIOSCIENCES INC-A0250,000+250,000$0$1.93M0.27%+$1.93M
Nuvation Bio Inc.(NUVB)508,846326,609-182,237$2.18M$1.86M0.26%-$327.8K
BioNTech SE(BNTX)19,61419,6140$1.74M$1.83M0.25%+$81.8K
COMPASS Pathways plc(CMPS)115,616115,6160$639.4K$1.64M0.23%+$996.6K
Humana Inc.(HUM)3,9853,9850$691.0K$1.58M0.22%+$892.0K
NEWAMSTERDAM PHARMA CO NV
ORDINARY SHARES
044,359+44,359$0$1.50M0.21%+$1.50M
VERASTEM INC246,093309,685+63,592$1.30M$1.18M0.16%-$121.3K
Madrigal Pharmaceuticals, Inc.(MDGL)1,7871,7870$935.4K$959.5K0.13%+$24.1K
UroGen Pharma Ltd.(URGN)24,50024,5000$440.5K$901.6K0.12%+$461.1K
BICYCLE THERAPEUTICS PLC-ADR201,890201,8900$936.8K$856.0K0.12%-$80.8K
XERIS BIOPHARMA HOLDINGS INC104,410104,4100$605.6K$826.9K0.11%+$221.3K
ABEONA THERAPEUTICS INC108,865108,8650$487.7K$672.8K0.09%+$185.1K
Inspire Medical Systems, Inc.(INSP)8,7728,7720$452.5K$391.3K0.05%-$61.1K
PROQR THERAPEUTICS NV
SHS EURO
188,807188,8070$305.9K$351.2K0.05%+$45.3K
ALDEYRA THERAPEUTICS INC155,709155,7090$263.1K$331.7K0.05%+$68.5K
AMICUS THERAPEUTICS INC
COM
1,113,0450-1,113,045$16.09M$0—-$16.09M
Denali Therapeutics Inc.(DNLI)234,5820-234,582$4.50M$0—-$4.50M
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Palo Alto Investors LP — 13F Holdings — Q2 2026 | TickerTrail