Fund Holdings — Palo Alto Investors LP

Total Portfolio Value
$540.39M
Total Bought
$99.54M
Total Sold
$79.63M
Net Transaction
+$19.91M
Filing Period:
Securities
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SharesValue ($K)
Q2 2025
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Q3 2025
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Change
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Q2 2025
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Q3 2025
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Weight (%)
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Change
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PTC THERAPEUTICS INC(PTCT)406,469862,613+456,14419,85252,9399.80%+33,087
DYNE THERAPEUTICS INC(DYN)264,9761,262,674+997,6982,52315,9732.96%+13,450
IOVANCE BIOTHERAPEUTICS INC(IOVA)3,429,3297,618,132+4,188,8035,89816,5313.06%+10,633
AMICUS THERAPEUTICS INC
COM
5,610,5135,367,798-242,71532,14842,2987.83%+10,150
ULTRAGENYX PHARMACEUTICAL IN(RARE)48,750369,531+320,7811,77311,1152.06%+9,343
GOSSAMER BIO INC(GOSS)5,739,0135,464,349-274,6647,05914,3712.66%+7,312
DISC MEDICINE INC(IRON)145,691224,300+78,6097,71614,8222.74%+7,106
SYNDAX PHARMACEUTICALS INC(SNDX)444,367654,930+210,5634,16110,0761.86%+5,915
PROTHENA CORP PLC
SHS
1,274,7531,324,028+49,2757,73812,9232.39%+5,185
CAREDX INC(CDNA)0316,204+316,20404,5980.85%+4,598
ANAPTYSBIO INC812,821673,520-139,30118,04520,6233.82%+2,579
DENALI THERAPEUTICS INC(DNLI)239,809408,006+168,1973,3555,9241.10%+2,569
NUVATION BIO INC(NUVB)772,6521,020,547+247,8951,5073,7760.70%+2,269
AGIOS PHARMACEUTICALS INC(AGIO)268,783265,497-3,2868,94010,6571.97%+1,717
MIRUM PHARMACEUTICALS INC(MIRM)64,70064,70003,2934,7430.88%+1,451
AVIDITY BIOSCIENCES INC118,886109,831-9,0553,3764,7850.89%+1,409
TAYSHA GENE THERAPIES INC(TSHA)1,246,0331,246,03302,8784,0750.75%+1,196
PYXIS ONCOLOGY INC(PYXS)1,037,4211,037,42101,1412,3030.43%+1,162
STOKE THERAPEUTICS INC(STOK)125,861105,427-20,4341,4292,4780.46%+1,049
TRAVERE THERAPEUTICS INC(TVTX)110,719110,71901,6392,6460.49%+1,008
ACLARIS THERAPEUTICS INC(ACRS)1,390,0281,566,840+176,8121,9742,9770.55%+1,003
NEUROCRINE BIOSCIENCES INC(NBIX)13,33418,117+4,7831,6762,5430.47%+867
ORUKA THERAPEUTICS INC(ORKA)059,985+59,98507910.15%+791
CRISPR THERAPEUTICS AG(CRSP)44,62541,226-3,3992,1712,6720.49%+501
PROQR THERAPEUTICS NV
SHS EURO
0188,807+188,80704020.07%+402
ALDEYRA THERAPEUTICS INC(ALDX)225,465225,46508641,1770.22%+313
BIOGEN INC(BIIB)205,759185,661-20,09825,84126,0074.81%+166
UROGEN PHARMA LTD(URGN)24,50024,50003364890.09%+153
HUMANA INC(HUM)3,9853,98509741,0370.19%+63
GENERATION BIO CO150,47515,047-135,42848920.02%+44
BICYCLE THERAPEUTICS PLC-ADR248,934221,071-27,8631,7301,7110.32%-19
AKARI THERAPEUTICS PLC-ADR(AKTX)146,024146,02401711470.03%-23
ABEONA THERAPEUTICS INC(ABEO)108,865108,86506185750.11%-44
EHEALTH INC(EHTH)1,577,8501,544,619-33,2316,8646,6571.23%-206
ALUMIS INC143,4370-143,4374300—-430
EDWARDS LIFESCIENCES CORP39,47333,640-5,8333,0872,6160.48%-471
VYNE THERAPEUTICS INC PIPE(YARW)445,4340-445,4347350—-735
BIONTECH SE-ADR(BNTX)25,20619,614-5,5922,6841,9340.36%-749
ALKERMES PLC(ALKS)221,021183,938-37,0836,3235,5181.02%-805
KARYOPHARM THERAPEUTICS INC(KPTI)187,9110-187,9118100—-810
NOVOCURE LTD(NVCR)962,3961,256,159+293,76317,13116,2303.00%-901
ALIGN TECHNOLOGY INC37,77245,735+7,9637,1515,7271.06%-1,424
ACADIA PHARMACEUTICALS INC2,563,2092,466,684-96,52555,28852,6399.74%-2,649
UNITED THERAPEUTICS CORP(UTHR)95,48258,186-37,29627,43724,3924.51%-3,045
BIOMARIN PHARMACEUTICAL INC(BMRN)840,470754,007-86,46346,20140,8377.56%-5,364
ALNYLAM PHARMACEUTICALS INC(ALNY)75,53532,320-43,21524,63114,7382.73%-9,893
STAAR SURGICAL CO(STAA)791,8790-791,87913,2880—-13,288
INSMED INC(INSM)865,113491,805-373,30887,06570,82513.11%-16,240
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Palo Alto Investors LP — 13F Holdings — Q3 2025 | TickerTrail